In 2022, some therapies to correct serious genetic disorders have been approved by medical regulators, and others have produced impressive clinical trial results
December 23, 2022
This year is full of gene replacement therapy Alleviating serious genetic diseases in children shows they are finally making good on their promise after a rocky decades.
“We’re curing kids from deadly diseases. Fantastic,” donald cohen told at UCLA new scientist A rare, life-threatening immune disorder called leukocyte adhesion deficiency was successfully reversed in nine children in May using gene replacement therapy.
Gene replacement therapy is used to correct the…